adeno-associated virus (AAV)-based gene therapy - Vertex, Affinia Therap
TSHA-120 - Taysha Gene Therapies
http://www.ncbi.nlm.nih.gov/pubmed/38507752
 
; A Reghan Foley; Ahmet Hoke; Beth Seremula; Bradley P Carlin; Carsten G Bönnemann; Charlotte J Sumner; Denis Rybin; Diana X Bharucha-Goebel; Diane Armao; Dimah Saade; Elizabeth M Kang; Eshetu Tesfaye; Gina Norato; Jessica A Chichester; Jody E Hooper; John D Heiss; Joshua J Todd; Laryssa A Huryn; Lawrence Charnas; Melissa Waite; Minal Jain; Payam Mohassel; Rachel M Bailey; Roberto Calcedo; Steven J Gray; Tanya Lehky; Thomas O Crawford; Thomas W Bouldin; Wadih M Zein
 
Mar 20, 2024